COMPOSITIONS FOR DELIVERY OF POLYNUCLEOTIDES

The present disclosure provides compositions for delivering polynucleotides and methods of use thereof for treating genetic diseases. The present disclosure also provides polynucleotide conjugates. The present disclosure further provides anti-transferrin receptor antibodies. La présente divulgation...

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Bibliographic Details
Main Authors WILLIAMS, Tishan, SALEH, Anthony, MARUSAK, Charles, KANG, Fu-An
Format Patent
LanguageEnglish
French
Published 29.06.2023
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Summary:The present disclosure provides compositions for delivering polynucleotides and methods of use thereof for treating genetic diseases. The present disclosure also provides polynucleotide conjugates. The present disclosure further provides anti-transferrin receptor antibodies. La présente divulgation concerne des compositions pour administrer des polynucléotides et des méthodes d'utilisation de celles-ci pour traiter des maladies génétiques. La présente divulgation concerne également des conjugués polynucléotidiques. La présente divulgation concerne en outre des anticorps anti-récepteur de transferrine.
Bibliography:Application Number: WO2022US53998