ENGINEERED CELLS FOR THERAPY
Strategies, systems, compositions, and methods for genetically modifying cells to include one or more loss-of-function modifications and/or to include one or more gain-of-function modifications, as well as modified cells (and compositions of such cells) that include one or more loss-of-function modi...
Saved in:
Main Authors | , |
---|---|
Format | Patent |
Language | English French |
Published |
15.12.2022
|
Subjects | |
Online Access | Get full text |
Cover
Loading…
Summary: | Strategies, systems, compositions, and methods for genetically modifying cells to include one or more loss-of-function modifications and/or to include one or more gain-of-function modifications, as well as modified cells (and compositions of such cells) that include one or more loss-of-function modifications and/or that include one or more gain-of-function modifications, are described. In certain aspects, such modified cells include at least one gain-of-function modification within a coding region of an essential gene.
L'invention concerne des stratégies, des systèmes, des compositions et des procédés permettant de modifier génétiquement des cellules en vue d'inclure une ou plusieurs modifications de perte de fonction et/ou d'inclure une ou plusieurs modifications de gain de fonction, ainsi que des cellules modifiées (et des compositions de telles cellules) qui comprennent une ou plusieurs modifications de perte de fonction et/ou qui comprennent une ou plusieurs modifications de gain de fonction. Dans certains aspects, de telles cellules modifiées comprennent au moins une modification de gain de fonction dans une région de codage d'un gène essentiel. |
---|---|
Bibliography: | Application Number: WO2022US27685 |