NOVEL COMPOUNDS FOR TREATMENT OF DISEASES RELATED TO DUX4 EXPRESSION

The present invention relates to compounds that act as DUX4 repressors, suitable for the treatment of diseases related to DUX4 expression, such as muscular dystrophies. It also relates to use of such compounds, or to methods of use of such compounds. La présente invention concerne des composés agiss...

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Bibliographic Details
Main Authors ANIGHORO, Andrew, PACE, Robert David Matthew, FOULKES, Gregory, RICHARDS, Jonathan Philip, LOKE, Pui Leng, DE MAEYER, Joris Herman, DAVENPORT, Adam James, DICKIE, Anthony Paul, RUEDA-ZUBIAURRE, Ainoa, ELLWOOD, Simon Fletcher, SCHNORRENBERG, Gerd, LECCI, Cristina
Format Patent
LanguageEnglish
French
Published 03.06.2021
Subjects
CHEMISTRY
HETEROCYCLIC COMPOUNDS
HUMAN NECESSITIES
HYGIENE
MEDICAL OR VETERINARY SCIENCE
METALLURGY
ORGANIC CHEMISTRY
PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES
SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS ORMEDICINAL PREPARATIONS
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Summary:The present invention relates to compounds that act as DUX4 repressors, suitable for the treatment of diseases related to DUX4 expression, such as muscular dystrophies. It also relates to use of such compounds, or to methods of use of such compounds. La présente invention concerne des composés agissant comme des répresseurs de DUX4 adaptés au traitement des maladies liées à l'expression de DUX4, telles que les dystrophies musculaires. La présente invention concerne également l'utilisation de tels composés, ou des procédés d'utilisation de tels composés.
Bibliography:Application Number: WO2020EP83803