TREATMENT OF PLIN1 RELATED DISEASES AND DISORDERS

Disclosed herein are compositions comprising an oligonucleotide that targets PLIN1. The oligonucleotide may include a small interfering RNA (siRNA) or an antisense oligonucleotide (ASO). Also provided herein are methods of treating conditions associated with PLIN1 gene mutations that include providi...

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Bibliographic Details
Main Authors CAJES, Brian, VEKICH, John, KLEINSTEIN, Sarah, BRUSE, Shannon, GOTTESMAN, Omri, ROZEMA, David, BUSKE, Paul, JAKUBOSKY, David, LEWIS, David
Format Patent
LanguageEnglish
Published 29.08.2024
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Summary:Disclosed herein are compositions comprising an oligonucleotide that targets PLIN1. The oligonucleotide may include a small interfering RNA (siRNA) or an antisense oligonucleotide (ASO). Also provided herein are methods of treating conditions associated with PLIN1 gene mutations that include providing an oligonucleotide that targets PLIN1 in a subject.
Bibliography:Application Number: US202218568170