ACIDOS NUCLEICOS ANTISENTIDO QUE INDUCEN LA OMISION DEL EXON 51

La presente memoria descriptiva proporciona un farmaco que provoca una omision altamente eficaz del exon 51 en el gen de la distrofina humana. La presente memoria descriptiva proporciona un oligomero antisentido que tiene una actividad para inducir la omision del exon 51 en el gen de la distrofina h...

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Bibliographic Details
Main Authors HASEGAWA, Saki, HONDA, Yu, FUKUI, Takahiro, AOKI, Yoshitsugu, MUCHIMA, Kaname, TAKEDA, Shin'ichi
Format Patent
LanguageSpanish
Published 07.02.2023
Subjects
BEER
BIOCHEMISTRY
CHEMISTRY
COMPOSITIONS THEREOF
CULTURE MEDIA
ENZYMOLOGY
HUMAN NECESSITIES
HYGIENE
MEDICAL OR VETERINARY SCIENCE
METALLURGY
MICROBIOLOGY
MICROORGANISMS OR ENZYMES
MUTATION OR GENETIC ENGINEERING
ORGANIC CHEMISTRY
PEPTIDES
PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES
PROPAGATING, PRESERVING OR MAINTAINING MICROORGANISMS
SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS ORMEDICINAL PREPARATIONS
SPIRITS
VINEGAR
WINE
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Summary:La presente memoria descriptiva proporciona un farmaco que provoca una omision altamente eficaz del exon 51 en el gen de la distrofina humana. La presente memoria descriptiva proporciona un oligomero antisentido que tiene una actividad para inducir la omision del exon 51 en el gen de la distrofina humana. The present specification provides a drug that causes highly-efficient skipping of exon 51 in the human dystrophin gene. The present specification provides an antisense oligomer having an activity to induce skipping of exon 51 in the human dystrophin gene.
Bibliography:Application Number: PE20220001832