COMPOSITIONS, DEVICES AND METHODS FOR TREATING FABRY DISEASE

Described herein are RPE cells engineered to secrete a GLA protein, as well as compositions, pharmaceutical preparations, and implantable devices comprising the engineered RPE cells, and methods of making and using the same for treating Fabry disease. En el presente documento se describen células RP...

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Main Authors BEAUREGARD Michael, JOHNSTON Erika, Ellen, OBERLI Matthias, Alexander, O'CONNOR Owen, CARMONA Guillaume, WOTTON Paul, Kevin, GONZALEZ Francisco, Caballero, YIN Zoe, VEISEH Omid, HEIDEBRECHT Richard, PERITT David, WAY Jeffrey, Charles, BARNEY Lauren, Emily, SEWELL Jared, A, SMITH Devyn, Mckinley, FLUHARTY Brian Richard, MAKINO Elina, MILLER Robert, James, PAPAKOSTA Marianthi
Format Patent
LanguageEnglish
Spanish
Published 22.10.2021
Subjects
CHEMICAL ASPECTS OF BANDAGES, DRESSINGS, ABSORBENT PADS, ORSURGICAL ARTICLES
DISINFECTION, STERILISATION, OR DEODORISATION OF AIR
HUMAN NECESSITIES
HYGIENE
MATERIALS FOR BANDAGES, DRESSINGS, ABSORBENT PADS, OR SURGICALARTICLES
MEDICAL OR VETERINARY SCIENCE
METHODS OR APPARATUS FOR STERILISING MATERIALS OR OBJECTS INGENERAL
PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES
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Summary:Described herein are RPE cells engineered to secrete a GLA protein, as well as compositions, pharmaceutical preparations, and implantable devices comprising the engineered RPE cells, and methods of making and using the same for treating Fabry disease. En el presente documento se describen células RPE modificadas por ingeniería genética para secretar una proteína GLA, así como composiciones, preparaciones farmacéuticas y dispositivos implantables que comprenden las células RPE modificadas por ingeniería genética, y métodos para fabricar y usar las mismas para tratar la enfermedad de Fabry.
Bibliography:Application Number: MX2021011754