COMPOSITIONS AND METHODS FOR THE TREATMENT OF HEMOGLOBINOPATHIES

• Main Authors: SCHMEDT CHRISTIAN, SNEAD JENNIFER, STEVENSON SUSAN C, MICKANIN CRAIG STEPHEN, YANG YI
• Format: Patent
• Language: English; Korean
• Published: 06.02.2024
• Subjects: BEER; BIOCHEMISTRY; CHEMISTRY; COMPOSITIONS THEREOF; CULTURE MEDIA; ENZYMOLOGY; HUMAN NECESSITIES; HYGIENE; MEDICAL OR VETERINARY SCIENCE; METALLURGY; MICROBIOLOGY; MICROORGANISMS OR ENZYMES; MUTATION OR GENETIC ENGINEERING; PROPAGATING, PRESERVING OR MAINTAINING MICROORGANISMS; SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS ORMEDICINAL PREPARATIONS; SPIRITS; VINEGAR; WINE

본 발명은 혈색소병증의 치료를 위한 게놈 편집 시스템, 시약 및 방법에 관한 것이다. The present invention is directed to genome editing systems, reagents and methods for the treatment of hemoglobinopathies.