TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS (ALS)

The present disclosure relates to AAVs encoding a SOD1 targeting polynucleotide which may be used to treat amyotrophic lateral sclerosis (ALS) and delivery methods for the treatment of spinal cord related disorders including ALS.

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Bibliographic Details
Main Authors Sah, Dinah Wen-Yee, Carroll Soper, Jenna, Patzke, Holger, Chen, Qingmin
Format Patent
LanguageEnglish
French
German
Published 30.10.2024
Subjects
HUMAN NECESSITIES
HYGIENE
MEDICAL OR VETERINARY SCIENCE
PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES
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Summary:The present disclosure relates to AAVs encoding a SOD1 targeting polynucleotide which may be used to treat amyotrophic lateral sclerosis (ALS) and delivery methods for the treatment of spinal cord related disorders including ALS.
Bibliography:Application Number: EP20240198662