PAH-MODULATING COMPOSITIONS AND METHODS

The disclosure provides, e.g., compositions, systems, and methods for targeting, editing, modifying, or manipulating a host cell's genome at one or more locations in a DNA sequence in a cell, tissue, or subject. Gene modifying systems for treating phenylketonuria (PKU) are described.

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Bibliographic Details
Main Authors ALTSHULER, Robert Charles, STEINBERG, Barrett Ethan, QUERBES, William, COTTA-RAMUSINO, Cecilia Giovanna Silvia, ROQUET, Nathaniel, SALOMON, William Edward, CITORIK, Robert James, KOTLAR, Randi Michelle, WANG, Zhan, RAY, Ananya, SANCHEZ, Carlos, KIM, Kyusik, CHEE, Daniel Raymond, APPONI, Luciano Henrique, BOTHMER, Anne Helen, MCALLISTER, Gregory David
Format Patent
LanguageEnglish
French
German
Published 17.07.2024
Subjects
BEER
BIOCHEMISTRY
CHEMISTRY
COMPOSITIONS THEREOF
CULTURE MEDIA
ENZYMOLOGY
METALLURGY
MICROBIOLOGY
MICROORGANISMS OR ENZYMES
MUTATION OR GENETIC ENGINEERING
PROPAGATING, PRESERVING OR MAINTAINING MICROORGANISMS
SPIRITS
VINEGAR
WINE
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Summary:The disclosure provides, e.g., compositions, systems, and methods for targeting, editing, modifying, or manipulating a host cell's genome at one or more locations in a DNA sequence in a cell, tissue, or subject. Gene modifying systems for treating phenylketonuria (PKU) are described.
Bibliography:Application Number: EP20220868281