METHODS OF TREATING OR INHIBITING ONSET OF HUNTINGTON'S DISEASE

• Main Authors: GOLDMAN STEVEN A, OSIPOVITCH MIKHAIL
• Format: Patent
• Language: Chinese; English
• Published: 13.04.2021
• Subjects: HUMAN NECESSITIES; HYGIENE; MEDICAL OR VETERINARY SCIENCE; PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES; SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS ORMEDICINAL PREPARATIONS

The disclosure herein relates generally to a method of treating or inhibiting onset of Huntington's disease. This method involves selecting a subject having or at risk of having Huntington's disease and administering to the subject one or modulators of one or more genes as described herein, or proteins encoded therefrom, under conditions effective to treat or inhibit onset of Huntington's disease in the subject. 本文的公开内容总体上涉及治疗或抑制亨廷顿病发作的方法。这种方法涉及选择患有亨廷顿病或者有患亨廷顿病风险的受试者，以及向所述受试者在对治疗或抑制所述受试者的亨廷顿病发作有效的条件下施用如本文所述的一种或多种基因或由其编码的蛋白质的一种或多种调节剂。