ANTISENSE NUCLEIC ACID INDUCING SKIPPING OF EXON 51

Provided is a drug that allows efficient skipping of the 51st exon in human dystrophin gene. Also provided is an antisense oligomer that has an activity of inducing skipping of the 51st exon in human dystrophin gene. L'invention concerne un médicament qui permet de sauter avec une grande effica...

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Main Authors HASEGAWA, SAKI, AOKI, YOSHITSUGU, MUCHIMA, KANAME, TAKEDA, SHIN'ICHI, HONDA, YU, FUKUI, TAKAHIRO
Format Patent
LanguageEnglish
French
Published 02.09.2021
Subjects
BEER
BIOCHEMISTRY
CHEMISTRY
COMPOSITIONS THEREOF
CULTURE MEDIA
ENZYMOLOGY
HUMAN NECESSITIES
HYGIENE
MEDICAL OR VETERINARY SCIENCE
METALLURGY
MICROBIOLOGY
MICROORGANISMS OR ENZYMES
MUTATION OR GENETIC ENGINEERING
ORGANIC CHEMISTRY
PEPTIDES
PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES
PROPAGATING, PRESERVING OR MAINTAINING MICROORGANISMS
SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS ORMEDICINAL PREPARATIONS
SPIRITS
VINEGAR
WINE
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Summary:Provided is a drug that allows efficient skipping of the 51st exon in human dystrophin gene. Also provided is an antisense oligomer that has an activity of inducing skipping of the 51st exon in human dystrophin gene. L'invention concerne un médicament qui permet de sauter avec une grande efficacité l'exon 51 dans le gène de la dystrophine humaine. L'invention concerne également un oligomère antisens qui présente une activité d'induction du saut de l'exon 51 dans le gène de la dystrophine humaine.
Bibliography:Application Number: CA20213173049