Antisense nucleic acid inducing skipping of exon 51

Provided is a drug that allows efficient skipping of the 51st exon in human dystrophin gene. Also provided is an antisense oligomer that has an activity of inducing skipping of the 51st exon in human dystrophin gene.

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Bibliographic Details
Main Authors HASEGAWA, Saki, HONDA, Yu, FUKUI, Takahiro, AOKI, Yoshitsugu, MUCHIMA, Kaname, TAKEDA, Shin'ichi
Format Patent
LanguageEnglish
Published 15.09.2022
Subjects
BEER
BIOCHEMISTRY
CHEMISTRY
COMPOSITIONS THEREOF
CULTURE MEDIA
ENZYMOLOGY
HUMAN NECESSITIES
HYGIENE
MEDICAL OR VETERINARY SCIENCE
METALLURGY
MICROBIOLOGY
MICROORGANISMS OR ENZYMES
MUTATION OR GENETIC ENGINEERING
ORGANIC CHEMISTRY
PEPTIDES
PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES
PROPAGATING, PRESERVING OR MAINTAINING MICROORGANISMS
SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS ORMEDICINAL PREPARATIONS
SPIRITS
VINEGAR
WINE
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Summary:Provided is a drug that allows efficient skipping of the 51st exon in human dystrophin gene. Also provided is an antisense oligomer that has an activity of inducing skipping of the 51st exon in human dystrophin gene.
Bibliography:Application Number: AU20210226089