A review of the clinical progression in six late onset Pompe disease (LOPD) patients following alglucosidase alfa cessation

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Bibliographic Details
Published inMolecular genetics and metabolism Vol. 138; no. 2; p. 107245
Main Authors Oldham, Andrew J., Stepien, Karolina M., Roberts, Mark E., Sharma, Reena
Format Journal Article
LanguageEnglish
Published Elsevier Inc 01.02.2023
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ISSN:1096-7192
1096-7206
DOI:10.1016/j.ymgme.2022.107245