A blinded randomized phase 2/3 study of the efficacy and safety of intravenous DNL310 (brain-penetrant enzyme replacement therapy) in MPS II

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Bibliographic Details
Published in	Molecular genetics and metabolism Vol. 135; no. 2; p. S55
Main Authors	Harris, Jeffrey, Zhu, Yuda, Ho, Judy, Chen, Charlene, Bakardjiev, Anna, Model, Fabian, Troyer, Matthew, Ho, Carole, Chin, Peter
Format	Journal Article
Language	English
Published	Elsevier Inc 01.02.2022
Online Access	Get full text

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ISSN:	1096-7192 1096-7206
DOI:	10.1016/j.ymgme.2021.11.134