Prospective longitudinal study of neurological disease trajectory in children living with late-infantile or juvenile onset of GM1 or GM2 gangliosidosis (PRONTO study)
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Published in | Molecular genetics and metabolism Vol. 135; no. 2; pp. S47 - S48 |
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Main Authors | , , , , , , |
Format | Journal Article |
Language | English |
Published |
Elsevier Inc
01.02.2022
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Online Access | Get full text |
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ISSN: | 1096-7192 1096-7206 |
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DOI: | 10.1016/j.ymgme.2021.11.113 |