Prospective longitudinal study of neurological disease trajectory in children living with late-infantile or juvenile onset of GM1 or GM2 gangliosidosis (PRONTO study)

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Bibliographic Details
Published inMolecular genetics and metabolism Vol. 135; no. 2; pp. S47 - S48
Main Authors Giugliani, Roberto, Heron, Benedicte, Jarnes, Jeanine R., Patterson, Marc C., Scarpa, Maurizio, Doppler, Emilie, Luzy, Cecile Paquet
Format Journal Article
LanguageEnglish
Published Elsevier Inc 01.02.2022
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ISSN:1096-7192
1096-7206
DOI:10.1016/j.ymgme.2021.11.113