Haemophilia A: health and economic burden of a rare disease in Portugal

Haemophilia A is a hereditary bleeding disorder, which has been considered rare and chronic. The burden of this disease in Portugal remains unknown. The aim of this study was to estimate the annualized cost and health burden of haemophilia A in Portugal. Financial support for the study was provided...

Full description

Saved in:
Bibliographic Details
Published inOrphanet journal of rare diseases Vol. 14; no. 211; pp. 1 - 11
Main Authors Café, Andreia, Carvalho, Manuela, Crato, Miguel, Faria, Miguel, Kjollerstrom, Paula, Oliveira, Cristina, Pinto, Patrícia Jesus Ribeiro, Salvado, Ramón, Dos Santos, Alexandra Aires, Silva, Catarina
Format Journal Article
LanguageEnglish
Published England BMC 04.09.2019
BioMed Central Ltd
BioMed Central
Subjects
Analysis
Burden
Care and treatment
Ciências Médicas
Clotting
Cost analysis
Cost-of-illness
Disability-adjusted life year
Economic aspects
Estimates
Haemophilia A
Health
Health care costs
Health economics
Hemophilia
Joint surgery
Males
Medical economics
Medical research
Medicina Básica
Patients
Portugal
Quality of life
Rare diseases
Risk factors
Science & Technology
Technical communication
Portugal
Haemophilia A
Health economics
Burden
Disability-adjusted life year
Portugal
Cost-of-illness
Online AccessGet full text

Cover

More Information
Summary:Haemophilia A is a hereditary bleeding disorder, which has been considered rare and chronic. The burden of this disease in Portugal remains unknown. The aim of this study was to estimate the annualized cost and health burden of haemophilia A in Portugal. Financial support for the study was provided by Roche. Eurotrials, Scientific Consultants (Contract Research Organization) was appointed by Roche to conduct the independent expert panel and perform the economic analysis.
Bibliography:ObjectType-Article-1
SourceType-Scholarly Journals-1
ObjectType-Feature-2
content type line 23
ISSN:1750-1172
1750-1172
DOI:10.1186/s13023-019-1175-5