Clinical progress in gene therapy: sustained partial correction of the bleeding disorder in patients suffering from severe hemophilia B

• Published in: Human gene therapy Vol. 23; no. 1; p. 4
• Main Authors: Vandendriessche, T, Chuah, M K
• Format: Journal Article
• Language: English
• Published: United States 01.01.2012
• Subjects: Clinical Trials as Topic; Dependovirus - immunology; Dependovirus - metabolism; Factor IX - immunology; Factor IX - metabolism; Factor VIII - immunology; Factor VIII - metabolism; Genetic Therapy; Genetic Vectors - immunology; Genetic Vectors - metabolism; Hemophilia A - immunology; Hemophilia A - metabolism; Hemophilia A - pathology; Hemophilia A - therapy; Hemophilia B - immunology; Hemophilia B - metabolism; Hemophilia B - pathology; Hemophilia B - therapy; Hemorrhage - immunology; Hemorrhage - metabolism; Hemorrhage - pathology; Hemorrhage - therapy; Hepatocytes - immunology; Hepatocytes - metabolism; Humans; Liver - immunology; Liver - metabolism
• ISSN: 1557-7422
• DOI: 10.1089/hum.2011.221