G.P.8.08 Codon optimisation of microdystrophin results in improvements in expression and physiological outcome in the mdx mouse following AAV8 gene transfer

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Published inNeuromuscular disorders : NMD Vol. 18; no. 9; p. 784
Main Authors Foster, H, Wells, D.J, Trollet, C, Athanasopoulos, T, Graham, I, Foster, K, Dickson, J.G
Format Journal Article
LanguageEnglish
Published Elsevier B.V 01.10.2008
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ISSN:0960-8966
1873-2364
DOI:10.1016/j.nmd.2008.06.207