Early treatment with laronidase improves clinical outcomes in patients with attenuated MPS I: Analysis of eight sibling pairs

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Bibliographic Details
Published in	Molecular genetics and metabolism Vol. 114; no. 2; pp. S93 - S94
Main Authors	Pleat, Rebecca, Al-Sannaa, Nouriya, Barbouth, Deborah S., Benhayoun, Youssef, Goizet, Cyril, Guelbert, Norberto, Jones, Simon A., Kyosen, Sandra, Martins, Ana Maria, Phornphutkul, Chanika, Reig, Celia, Holder, Iva Ivanovska, Fallet, Shari
Format	Journal Article
Language	English
Published	Elsevier Inc 01.02.2015
Online Access	Get full text

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ISSN:	1096-7192 1096-7206
DOI:	10.1016/j.ymgme.2014.12.208