Mini-COMET study: Effects of repeat avalglucosidase alfa dosing on ptosis in participants with infantile-onset Pompe disease (IOPD) who were previously treated with alglucosidase alfa

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Bibliographic Details
Published inMolecular genetics and metabolism Vol. 132; no. 2; pp. S31 - S32
Main Authors Davison, James, Brassier, Anaïs, Broomfield, Alexander, Chien, Yin-Hsiu, Hahn, Si Houn, Kronn, David, Kumada, Satoko, Labarthe, François, Ohki, Hirotaka, Pichard, Samia, Prakalapakorn, S. Grace, Haack, Kristina An, Johnson, Judith, Meng, Xianzhang
Format Journal Article
LanguageEnglish
Published Elsevier Inc 01.02.2021
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ISSN:1096-7192
1096-7206
DOI:10.1016/j.ymgme.2020.12.058