Long-term results of ENGAGE: a phase 3, randomized, double‑blind, placebo-controlled, multi‑center study investigating the efficacy and safety of eliglustat in adults with type 1 Gaucher disease

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Published inMolecular genetics and metabolism Vol. 120; no. 1-2; pp. S97 - S98
Main Authors Mistry, Pramod K, Lukina, Elena, Turkia, Hadhami Ben, Shankar, Suma, Feldman, Hagit Baris, Ghosn, Marwan, Mehta, Atul, Packman, Seymour, Lau, Heather, Petakov, Milan, Assouline, Sarit, Balwani, Manisha, Danda, Sumita, Hadjiev, Evgueniy, Ortega, Andres, Wu, Yaoshi, Gaemers, Sebastiaan J.M., Judith Peterschmitt, M.
Format Journal Article
LanguageEnglish
Published Elsevier Inc 01.01.2017
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ISSN:1096-7192
1096-7206
DOI:10.1016/j.ymgme.2016.11.243