LYSOSOMAL TARGETING OF ENZYMES, AND USES THEREOF
The invention provides compositions and methods for effective lysosomal targeting mediated by PCSK9. In particular, the compositions and methods provided by the invention may be used to treat lysosomal storage diseases such as Pompe Disease and Sanfilippo Syndrome Type B, and they may be used for ta...
Saved in:
Main Authors | , |
---|---|
Format | Patent |
Language | English French |
Published |
28.04.2016
|
Subjects | |
Online Access | Get full text |
Cover
Loading…
Be the first to leave a comment!