COMPOUNDS AND METHODS FOR MODULATING SPLICING

• Main Authors: Agrawal, Anant A, Seiler, Michael W, Vaillancourt, Frederic, Smith, Peter, Prajapati, Sudeep, Reynolds, Dominic, Leger, Serge
• Format: Patent
• Language: English
• Published: 22.08.2024
• Subjects: CHEMISTRY; HETEROCYCLIC COMPOUNDS; HUMAN NECESSITIES; HYGIENE; MEDICAL OR VETERINARY SCIENCE; METALLURGY; ORGANIC CHEMISTRY; PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES

The present disclosure features compounds and related compositions that, inter alia, modulate nucleic acid splicing, e.g., splicing of a pre-mRNA, as well as methods of use thereof.