COMPOSITIONS AND METHODS FOR GENE EDITING FOR HEMOPHILIA A
Provided include materials and methods for treating Hemophilia A in a subject ex vivo or in vivo. Also provided include materials and methods for knocking in a FVIII-encoding gene in a genome, in particular the locus of albumin gene.
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Main Author | |
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Format | Patent |
Language | English |
Published |
17.03.2022
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Subjects | |
Online Access | Get full text |
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