COMPOUNDS FOR TREATING SPINAL MUSCULAR ATROPHY
Provided herein are compounds, compositions thereof and uses therewith for treating spinal muscular atrophy.
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Format | Patent |
Language | English |
Published |
12.12.2019
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Subjects | |
Online Access | Get full text |
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Abstract | Provided herein are compounds, compositions thereof and uses therewith for treating spinal muscular atrophy. |
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AbstractList | Provided herein are compounds, compositions thereof and uses therewith for treating spinal muscular atrophy. |
Author | GREEN, Luke QI, Hongyan YANG, Tianle PINARD, Emmanuel NARYSHKIN, Nikolai WELCH, Ellen ZHAO, Xin NARASIMHAN, Jana RATNI, Hasane TURPOFF, Anthony A WOLL, Matthew G WEETALL, Marla L CHOI, Soongyu ZHANG, Xiaoyan DAKKA, Amal KARP, Gary Mitchell ZHANG, Nanjing |
Author_xml | – fullname: YANG, Tianle – fullname: ZHANG, Nanjing – fullname: PINARD, Emmanuel – fullname: WOLL, Matthew G – fullname: KARP, Gary Mitchell – fullname: WELCH, Ellen – fullname: WEETALL, Marla L – fullname: ZHANG, Xiaoyan – fullname: GREEN, Luke – fullname: DAKKA, Amal – fullname: RATNI, Hasane – fullname: NARYSHKIN, Nikolai – fullname: CHOI, Soongyu – fullname: NARASIMHAN, Jana – fullname: QI, Hongyan – fullname: TURPOFF, Anthony A – fullname: ZHAO, Xin |
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RelatedCompanies | PTC Therapeutics, Inc F. Hoffmann-La Roche AG |
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Snippet | Provided herein are compounds, compositions thereof and uses therewith for treating spinal muscular atrophy. |
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Title | COMPOUNDS FOR TREATING SPINAL MUSCULAR ATROPHY |
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