COMPOUNDS FOR TREATING SPINAL MUSCULAR ATROPHY

Provided herein are compounds, compositions thereof and uses therewith for treating spinal muscular atrophy.

Saved in:
Bibliographic Details
Main Authors YANG, Tianle, ZHANG, Nanjing, PINARD, Emmanuel, WOLL, Matthew G, KARP, Gary Mitchell, WELCH, Ellen, WEETALL, Marla L, ZHANG, Xiaoyan, GREEN, Luke, DAKKA, Amal, RATNI, Hasane, NARYSHKIN, Nikolai, CHOI, Soongyu, NARASIMHAN, Jana, QI, Hongyan, TURPOFF, Anthony A, ZHAO, Xin
Format Patent
LanguageEnglish
Published 12.12.2019
Subjects
Online AccessGet full text

Cover

Loading…
Abstract Provided herein are compounds, compositions thereof and uses therewith for treating spinal muscular atrophy.
AbstractList Provided herein are compounds, compositions thereof and uses therewith for treating spinal muscular atrophy.
Author GREEN, Luke
QI, Hongyan
YANG, Tianle
PINARD, Emmanuel
NARYSHKIN, Nikolai
WELCH, Ellen
ZHAO, Xin
NARASIMHAN, Jana
RATNI, Hasane
TURPOFF, Anthony A
WOLL, Matthew G
WEETALL, Marla L
CHOI, Soongyu
ZHANG, Xiaoyan
DAKKA, Amal
KARP, Gary Mitchell
ZHANG, Nanjing
Author_xml – fullname: YANG, Tianle
– fullname: ZHANG, Nanjing
– fullname: PINARD, Emmanuel
– fullname: WOLL, Matthew G
– fullname: KARP, Gary Mitchell
– fullname: WELCH, Ellen
– fullname: WEETALL, Marla L
– fullname: ZHANG, Xiaoyan
– fullname: GREEN, Luke
– fullname: DAKKA, Amal
– fullname: RATNI, Hasane
– fullname: NARYSHKIN, Nikolai
– fullname: CHOI, Soongyu
– fullname: NARASIMHAN, Jana
– fullname: QI, Hongyan
– fullname: TURPOFF, Anthony A
– fullname: ZHAO, Xin
BookMark eNrjYmDJy89L5WTQc_b3DfAP9XMJVnDzD1IICXJ1DPH0c1cIDvD0c_RR8A0Ndg71cQxScAwJ8g_wiORhYE1LzClO5YXS3AzKbq4hzh66qQX58anFBYnJqXmpJfGhwUYGhpbG5qbmpgaOhsbEqQIAmvkozA
ContentType Patent
DBID EVB
DatabaseName esp@cenet
DatabaseTitleList
Database_xml – sequence: 1
  dbid: EVB
  name: esp@cenet
  url: http://worldwide.espacenet.com/singleLineSearch?locale=en_EP
  sourceTypes: Open Access Repository
DeliveryMethod fulltext_linktorsrc
Discipline Medicine
Chemistry
Sciences
ExternalDocumentID US2019375750A1
GroupedDBID EVB
ID FETCH-epo_espacenet_US2019375750A13
IEDL.DBID EVB
IngestDate Fri Jul 19 12:57:27 EDT 2024
IsOpenAccess true
IsPeerReviewed false
IsScholarly false
Language English
LinkModel DirectLink
MergedId FETCHMERGED-epo_espacenet_US2019375750A13
Notes Application Number: US201916541401
OpenAccessLink https://worldwide.espacenet.com/publicationDetails/biblio?FT=D&date=20191212&DB=EPODOC&CC=US&NR=2019375750A1
ParticipantIDs epo_espacenet_US2019375750A1
PublicationCentury 2000
PublicationDate 20191212
PublicationDateYYYYMMDD 2019-12-12
PublicationDate_xml – month: 12
  year: 2019
  text: 20191212
  day: 12
PublicationDecade 2010
PublicationYear 2019
RelatedCompanies PTC Therapeutics, Inc
F. Hoffmann-La Roche AG
RelatedCompanies_xml – name: PTC Therapeutics, Inc
– name: F. Hoffmann-La Roche AG
Score 3.2469192
Snippet Provided herein are compounds, compositions thereof and uses therewith for treating spinal muscular atrophy.
SourceID epo
SourceType Open Access Repository
SubjectTerms CHEMISTRY
HETEROCYCLIC COMPOUNDS
HUMAN NECESSITIES
HYGIENE
MEDICAL OR VETERINARY SCIENCE
METALLURGY
ORGANIC CHEMISTRY
PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES
Title COMPOUNDS FOR TREATING SPINAL MUSCULAR ATROPHY
URI https://worldwide.espacenet.com/publicationDetails/biblio?FT=D&date=20191212&DB=EPODOC&locale=&CC=US&NR=2019375750A1
hasFullText 1
inHoldings 1
isFullTextHit
isPrint
link http://utb.summon.serialssolutions.com/2.0.0/link/0/eLvHCXMwfV1LS8NAEB5KFfWmVfFRZUHJLVqTmDSHIOkmMUrzIA-pp5JNtyBIWmzEv-9sSLWn3nZ3YF8ws_PtvABuTaPgbG6K6mUalzW90GRWDEtZGRYGK0tV5YX40A9C3c-118njpAOf61iYJk_oT5McETmqRH6vG3m9_P_EchrfytU9-8ChxZOXWY7UomMEHyiKJWdkuXHkRFSi1MpTKUwammqgbjKwESvtCEVaZNp330YiLmW5-ah4h7Ab43xVfQQdXvVgn65rr_VgL2hN3thsuW91DHc0CuIoD52UIHYjWeLa2Uv4TFKE5vaYBHlK87GdEDtLoth_P4Ebz82oL-PC079zTvN0c5fqKXSrRcXPgJhqMZwxDaGSYmqGsGxyw5zrChvoXMRMnUN_20wX28mXcCC6wkfjQelDt_765lf40tbsurmgX4KRfIs
link.rule.ids 230,309,786,891,25594,76906
linkProvider European Patent Office
linkToHtml http://utb.summon.serialssolutions.com/2.0.0/link/0/eLvHCXMwfV1LS8NAEB5KFetNq-KjakDJLVqTmDSHIOkmNdW8yEPaU8jGLQiSFhvx7zsbWu2pt2UHZh8wM_vtvABuDb1gdGbw7mUqk1StUCVaDEpJHhQ6LUtFYQX_0PcDzc3Ul8njpAWf61yYpk7oT1McESWqRHmvG329-P_EspvYyuU9_cCp-dMoNW1xhY4RfKAqFu2h6UShHRKREDNLxCBuaIqOb5O-hVhpR-f1efnj6W3I81IWm0ZldAC7EfKr6kNosaoLHbLuvdaFPX_l8sbhSvqWR3BHQj8Ks8BOBMRuQho7VjoOnoUEobnlCX6WkMyzYsFK4zByp8dwM3JS4kq4cP53zjxLNnepnEC7mlfsFARDKQbvVEWoJBuqzj2bTDdmmkz7GuM5U2fQ28bpfDv5Gjpu6nu5Nw5eL2Cfk3i8xoPcg3b99c0u0erW9Kq5rF99z394
openUrl ctx_ver=Z39.88-2004&ctx_enc=info%3Aofi%2Fenc%3AUTF-8&rfr_id=info%3Asid%2Fsummon.serialssolutions.com&rft_val_fmt=info%3Aofi%2Ffmt%3Akev%3Amtx%3Apatent&rft.title=COMPOUNDS+FOR+TREATING+SPINAL+MUSCULAR+ATROPHY&rft.inventor=YANG%2C+Tianle&rft.inventor=ZHANG%2C+Nanjing&rft.inventor=PINARD%2C+Emmanuel&rft.inventor=WOLL%2C+Matthew+G&rft.inventor=KARP%2C+Gary+Mitchell&rft.inventor=WELCH%2C+Ellen&rft.inventor=WEETALL%2C+Marla+L&rft.inventor=ZHANG%2C+Xiaoyan&rft.inventor=GREEN%2C+Luke&rft.inventor=DAKKA%2C+Amal&rft.inventor=RATNI%2C+Hasane&rft.inventor=NARYSHKIN%2C+Nikolai&rft.inventor=CHOI%2C+Soongyu&rft.inventor=NARASIMHAN%2C+Jana&rft.inventor=QI%2C+Hongyan&rft.inventor=TURPOFF%2C+Anthony+A&rft.inventor=ZHAO%2C+Xin&rft.date=2019-12-12&rft.externalDBID=A1&rft.externalDocID=US2019375750A1