BICALUTAMIDE ANALOGS OR (S)-BICALUTAMIDE AS EXOCYTOSIS ACTIVATING COMPOUNDS FOR USE IN THE TREATMENT OF A LYSOSOMAL STORAGE DISORDER OR GLYCOGENOSIS

The invention provides a therapy for lysosomal storage diseases and glycogenosis by treatment with compounds that promote exocytosis, preferably lysosomal exocytosis. The treatment of cells from patients affected by different lysosomal storage disorders with exocytosis activating compounds leads to...

Full description

Saved in:
Bibliographic Details
Main Authors FARRERA-SINFREU, JOSEP, GORT MAS, LAURA, MATALONGA BORREL, LESLIE, FERRER MONTIEL, ANTONIO, PONSATI OBIOLS, BERTA, RIBES RUBIO, ANTONIA, PASCUAL MARTINEZ, ROBERTO
Format Patent
LanguageEnglish
Published 05.02.2021
Online AccessGet full text

Cover

Abstract The invention provides a therapy for lysosomal storage diseases and glycogenosis by treatment with compounds that promote exocytosis, preferably lysosomal exocytosis. The treatment of cells from patients affected by different lysosomal storage disorders with exocytosis activating compounds leads to a decrease in the accumulation of toxic substrate in the lysosomes, thus allowing the treatment, prevention and relief of the symptoms of many lysosomal storage disorders.
AbstractList The invention provides a therapy for lysosomal storage diseases and glycogenosis by treatment with compounds that promote exocytosis, preferably lysosomal exocytosis. The treatment of cells from patients affected by different lysosomal storage disorders with exocytosis activating compounds leads to a decrease in the accumulation of toxic substrate in the lysosomes, thus allowing the treatment, prevention and relief of the symptoms of many lysosomal storage disorders.
Author PONSATI OBIOLS, BERTA
FARRERA-SINFREU, JOSEP
RIBES RUBIO, ANTONIA
FERRER MONTIEL, ANTONIO
PASCUAL MARTINEZ, ROBERTO
GORT MAS, LAURA
MATALONGA BORREL, LESLIE
Author_xml – fullname: FARRERA-SINFREU, JOSEP
– fullname: GORT MAS, LAURA
– fullname: MATALONGA BORREL, LESLIE
– fullname: FERRER MONTIEL, ANTONIO
– fullname: PONSATI OBIOLS, BERTA
– fullname: RIBES RUBIO, ANTONIA
– fullname: PASCUAL MARTINEZ, ROBERTO
BookMark eNqFjb1uAjEQhK-AIgReIdoSCiR-Gig3vj1jyfYi7x7iqtMpcqroQIJH4YEBKQ0V1RTzzTejYtCf-vxR3L6dQV8rBlcSYETPVoATTGU2f-0E6MimURYngEbdAdVFC4bDnutYClSPXS0ELoLuCDQRaqCowBUg-EZYOKAHUU5oCUonnEpKzz_rG8OW4tM-Loa_3d8lT_7zs_iqSM1uns-nNl_O3U_u87UNzXKz2i7WuH4L3AFfYkJb
ContentType Patent
DBID EVB
DatabaseName esp@cenet
DatabaseTitleList
Database_xml – sequence: 1
  dbid: EVB
  name: esp@cenet
  url: http://worldwide.espacenet.com/singleLineSearch?locale=en_EP
  sourceTypes: Open Access Repository
DeliveryMethod fulltext_linktorsrc
Discipline Medicine
Chemistry
Sciences
ExternalDocumentID MY182903A
GroupedDBID EVB
ID FETCH-epo_espacenet_MY182903A3
IEDL.DBID EVB
IngestDate Fri Jul 19 12:47:53 EDT 2024
IsOpenAccess true
IsPeerReviewed false
IsScholarly false
Language English
LinkModel DirectLink
MergedId FETCHMERGED-epo_espacenet_MY182903A3
Notes Application Number: MY2016PI00977
OpenAccessLink https://worldwide.espacenet.com/publicationDetails/biblio?FT=D&date=20210205&DB=EPODOC&CC=MY&NR=182903A
ParticipantIDs epo_espacenet_MY182903A
PublicationCentury 2000
PublicationDate 20210205
PublicationDateYYYYMMDD 2021-02-05
PublicationDate_xml – month: 02
  year: 2021
  text: 20210205
  day: 05
PublicationDecade 2020
PublicationYear 2021
RelatedCompanies BCN PEPTIDES, S.A
RelatedCompanies_xml – name: BCN PEPTIDES, S.A
Score 3.308368
Snippet The invention provides a therapy for lysosomal storage diseases and glycogenosis by treatment with compounds that promote exocytosis, preferably lysosomal...
SourceID epo
SourceType Open Access Repository
Title BICALUTAMIDE ANALOGS OR (S)-BICALUTAMIDE AS EXOCYTOSIS ACTIVATING COMPOUNDS FOR USE IN THE TREATMENT OF A LYSOSOMAL STORAGE DISORDER OR GLYCOGENOSIS
URI https://worldwide.espacenet.com/publicationDetails/biblio?FT=D&date=20210205&DB=EPODOC&locale=&CC=MY&NR=182903A
hasFullText 1
inHoldings 1
isFullTextHit
isPrint
link http://utb.summon.serialssolutions.com/2.0.0/link/0/eLvHCXMwdV1Lb8IwDI4Ym7bdNvZ-IB8mtB2qFfpgHNAU2rR0og1qAqInREs77QJodNof2Q9eUpU9DiiXKJYcxZFjO7G_IHSXxKlwKuK5Yj7Ni6sbQ5mZnURpa6I1ZzNdz2Rxsh-Y_ZH-MjEmFfS6qYUpcEI_C3BEoVGJ0Pe8OK9Xv5dYdpFbuX6M38TQ8tnhXbtRRscyflGNht3rkiG1qdWwrK4fNYJQKHmro2p4B-0KH7otc7_IuCdLUlZ_7YlzhPaGgtUiP0aVdFFDB9bm27Ua2vfL127RLRVvfYK-ehK3YMSx79kEcIAH1GVAQ7hnD8p_GgMyoVbEKfMYyByRMeZe4IJF_SEdBTYDEfjBiBHwAuB9AjwkmEtMf6AOYBhEjDLq4wEwTkPsErA9JkJFEsr53EFkUZcEkvspqjuEW31FLG_6I8ipH5Vi0M5QdbFcpBcITD2OWxLRR-0ketzUYlVLs8ycqYneycx5donOtzC52kq5RodyL4rkZuMGVfP3j_RW2O48rhdy_wZ5wpSH
link.rule.ids 230,309,783,888,25578,76884
linkProvider European Patent Office
linkToHtml http://utb.summon.serialssolutions.com/2.0.0/link/0/eLvHCXMwdV1bT8IwFG4QjfimeL_geTBEHxYHuwgPxJStjOm2krUQ9kTY2IwvQGTGP-IPtl3Ay4PpS9OTnKanOW2_9pyvCN0kcSoOFfFMMVuz4urGUKZmO1EeNFEa06muZzI52Q_M_lB_GhvjEnrZ5MIUPKEfBTmi8KhE-HterNfLn0ssu4itXN3Hr6Jp8djjHbu-RscSv6hG3e52yIDa1KpbVseP6kEonLzZVjW8hbbF-bolSfbJqCtTUpa_95PePtoZCFXz_ACV0nkVVazNt2tVtOuvX7tFde14q0P02ZW8BUOOfdcmgAPsUYcBDeGW3Sl_ZQzImFoRp8xlIGNERpi7gQMW9Qd0GNgMBPCDISPgBsD7BHhIMJec_kB7gMGLGGXUxx4wTkPsELBdJqAiCWV_jhdZ1CGB1H6Eaj3Crb4ihjf5NuTEj9Zm0I5Reb6Yp6cITD2Om5LRR20netzQYlVLs8ycqonezsxZdoZO_lFy_q_kGlX63Pcmnhs8X6A9OS9FoLNxicr523t6JfbxPK4Vc_AFmtWXdw
openUrl ctx_ver=Z39.88-2004&ctx_enc=info%3Aofi%2Fenc%3AUTF-8&rfr_id=info%3Asid%2Fsummon.serialssolutions.com&rft_val_fmt=info%3Aofi%2Ffmt%3Akev%3Amtx%3Apatent&rft.title=BICALUTAMIDE+ANALOGS+OR+%28S%29-BICALUTAMIDE+AS+EXOCYTOSIS+ACTIVATING+COMPOUNDS+FOR+USE+IN+THE+TREATMENT+OF+A+LYSOSOMAL+STORAGE+DISORDER+OR+GLYCOGENOSIS&rft.inventor=FARRERA-SINFREU%2C+JOSEP&rft.inventor=GORT+MAS%2C+LAURA&rft.inventor=MATALONGA+BORREL%2C+LESLIE&rft.inventor=FERRER+MONTIEL%2C+ANTONIO&rft.inventor=PONSATI+OBIOLS%2C+BERTA&rft.inventor=RIBES+RUBIO%2C+ANTONIA&rft.inventor=PASCUAL+MARTINEZ%2C+ROBERTO&rft.date=2021-02-05&rft.externalDBID=A&rft.externalDocID=MY182903A