EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY

인간 디스트로핀 유전자에서 선택된 표적 부위에 결합하여 엑손 44 스키핑을 유도할 수 있는 인간 안티센스 분자가 기재된다. Antisense molecules capable of binding to a selected target site in the human dystrophin gene to induce exon 44 skipping are described....

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Bibliographic Details
Main Authors SCHNELL FRED JOSEPH, FRANK DIANE ELIZABETH, BESTWICK RICHARD K
Format Patent
LanguageEnglish
Korean
Published 04.08.2023
Subjects
BEER
BIOCHEMISTRY
CHEMISTRY
COMPOSITIONS THEREOF
CULTURE MEDIA
ENZYMOLOGY
HUMAN NECESSITIES
HYGIENE
MEDICAL OR VETERINARY SCIENCE
METALLURGY
MICROBIOLOGY
MICROORGANISMS OR ENZYMES
MUTATION OR GENETIC ENGINEERING
PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES
PROPAGATING, PRESERVING OR MAINTAINING MICROORGANISMS
SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS ORMEDICINAL PREPARATIONS
SPIRITS
VINEGAR
WINE
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Summary:인간 디스트로핀 유전자에서 선택된 표적 부위에 결합하여 엑손 44 스키핑을 유도할 수 있는 인간 안티센스 분자가 기재된다. Antisense molecules capable of binding to a selected target site in the human dystrophin gene to induce exon 44 skipping are described.
Bibliography:Application Number: KR20237024770