LYSOSOMAL TARGETING AND USES THEREOF

The invention provides compositions and methods for effective lysosomal targeting mediated by SORT1. In particular, the compositions and methods provided by the invention may be used to treat lysosomal storage diseases such as Sanfilippo syndrome type B.

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Main Authors NORTON, Angela W, CONCINO, Michael F, STRACK-LOGUE, Bettina, ISKENDERIAN, Andrea, HOLMES, Kevin, ZHANG, Bohong, MEIYAPPAN, Muthuraman, FENG, Jianwen, PAN, Jing
Format Patent
LanguageEnglish
French
German
Published 26.07.2017
Subjects
HUMAN NECESSITIES
HYGIENE
MEDICAL OR VETERINARY SCIENCE
PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES
SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS ORMEDICINAL PREPARATIONS
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Abstract The invention provides compositions and methods for effective lysosomal targeting mediated by SORT1. In particular, the compositions and methods provided by the invention may be used to treat lysosomal storage diseases such as Sanfilippo syndrome type B.
AbstractList The invention provides compositions and methods for effective lysosomal targeting mediated by SORT1. In particular, the compositions and methods provided by the invention may be used to treat lysosomal storage diseases such as Sanfilippo syndrome type B.
Author NORTON, Angela W
MEIYAPPAN, Muthuraman
ZHANG, Bohong
ISKENDERIAN, Andrea
FENG, Jianwen
CONCINO, Michael F
STRACK-LOGUE, Bettina
PAN, Jing
HOLMES, Kevin
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– fullname: ISKENDERIAN, Andrea
– fullname: HOLMES, Kevin
– fullname: ZHANG, Bohong
– fullname: MEIYAPPAN, Muthuraman
– fullname: FENG, Jianwen
– fullname: PAN, Jing
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DocumentTitleAlternate CIBLAGE LYSOSOMIAL ET UTILISATION CORRESPONDANTE
LYSOSOMALES TARGETING UND VERWENDUNGEN DAVON
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Snippet The invention provides compositions and methods for effective lysosomal targeting mediated by SORT1. In particular, the compositions and methods provided by...
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SubjectTerms HUMAN NECESSITIES
HYGIENE
MEDICAL OR VETERINARY SCIENCE
PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES
SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS ORMEDICINAL PREPARATIONS
Title LYSOSOMAL TARGETING AND USES THEREOF
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