COMPOUNDS FOR TREATING SPINAL MUSCULAR ATROPHY

Provided herein are compounds, compositions thereof and uses therewith for treating spinal muscular atrophy. F///, x-onIntron 6 Exn Intron 7 Eo U Pre-mRNA Spliced mRNA Luciferase +Compound A Activity Exn 6xon Exon 7Exon 8 luc + Yes -Compound Stop Exon 6 Exon 8 luc + No Figure 1

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Bibliographic Details
Main Authors YANG, Tianle, ZHANG, Nanjing, PINARD, Emmanuel, CHOI, Soongya, WOLL, Matthew G, KARP, Gary Mitchell, WELCH, Ellen, WEETALL, Marla L, ZHANG, Xiaoyan, GREEN, Luke, DAKKA, Amal, RATNI, Hasane, NARYSHKIN, Nikolai, NARASIMHAN, Jana, QI, Hongyan, TURPOFF, Anthony A, ZHAO, Xin
Format Patent
LanguageEnglish
Published 30.05.2019
Subjects
AGRICULTURE
ANIMAL HUSBANDRY
BIOCIDES, e.g. AS DISINFECTANTS, AS PESTICIDES, AS HERBICIDES
CHEMISTRY
FISHING
FORESTRY
HETEROCYCLIC COMPOUNDS
HUMAN NECESSITIES
HUNTING
HYGIENE
MEDICAL OR VETERINARY SCIENCE
METALLURGY
ORGANIC CHEMISTRY
PEST REPELLANTS OR ATTRACTANTS
PLANT GROWTH REGULATORS
PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES
PRESERVATION OF BODIES OF HUMANS OR ANIMALS OR PLANTS OR PARTSTHEREOF
TRAPPING
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Summary:Provided herein are compounds, compositions thereof and uses therewith for treating spinal muscular atrophy. F///, x-onIntron 6 Exn Intron 7 Eo U Pre-mRNA Spliced mRNA Luciferase +Compound A Activity Exn 6xon Exon 7Exon 8 luc + Yes -Compound Stop Exon 6 Exon 8 luc + No Figure 1
Bibliography:Application Number: AU20170204248