P.383Antisense oligonucleotides therapy for COL6-related congenital muscular dystrophy

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Published inNeuromuscular disorders : NMD Vol. 29; p. S193
Main Authors Aguti, S., Bolduc, V., Sarathy, A., Zou, Y., Bönnemann, C., Muntoni, F., Zhou, H.
Format Journal Article
LanguageEnglish
Published Elsevier B.V 01.10.2019
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Author Bönnemann, C.
Aguti, S.
Sarathy, A.
Muntoni, F.
Bolduc, V.
Zou, Y.
Zhou, H.
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  organization: University College London, London, UK
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Title P.383Antisense oligonucleotides therapy for COL6-related congenital muscular dystrophy
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