Ongoing therapeutic trials and outcome measures for Duchenne muscular dystrophy - Govoni, Alessandra; Magri, Francesca; Brajkovic, Simona; Zanetta, Chiara; Faravelli, Irene; Corti, Stefania; Bresolin, Nereo; Comi, Giacomo P (Cellular and molecular life sciences : CMLS, 2013)
Keywords: Animals; Becker's muscular dystrophy; Biochemistry; Biomarkers - blood; Biomedical and Life Sciences; Biomedicine; Cell Biology; Cell therapy; Clinical outcomes; Clinical trials; Clinical Trials as Topic - methods; Degeneration; Drug Therapy - methods; Duchenne's muscular dystrophy; Dystrophy; Exon skipping; exons; experimental design; Gene therapy; Genetic disorders; Humans; Immunomodulation; Life Sciences; muscle tissues; Muscular dystrophy; Muscular Dystrophy, Duchenne - blood; Muscular Dystrophy, Duchenne - physiopathology; Muscular Dystrophy, Duchenne - therapy; Outcome Assessment, Health Care - methods; Reproducibility of Results; Review; Stem Cell Transplantation - methods; tissue degeneration; Walking - physiology; Outcome measures; Clinical trial; Readthrough; Duchenne muscular dystrophy; Exon skipping; New therapeutic approaches