Gene Therapy in Rare Respiratory Diseases: What Have We Learned So Far? - Bañuls, Lucía; Pellicer, Daniel; Castillo, Silvia; Navarro-García, María Mercedes; Magallón, María; González, Cruz; Dasí, Francisco (Journal of clinical medicine, 2020)
Keywords: Clinical medicine; Clinical trials; CRISPR; Cystic fibrosis; Gene expression; Gene therapy; Genetic engineering; Genome editing; Genomes; Immune system; Lungs; Mutation; Respiratory diseases; Review; Vectors (Biology); Viruses; gene therapy; alpha-1-antitrypsin deficit; rare respiratory diseases; cystic fibrosis; primary ciliary dyskinesia