Cryptic exon activation causes dystrophinopathy in two Chinese families - Jin, Ming; Li, Jin-Jing; Xu, Guo-Rong; Wang, Ning; Wang, Zhi-Qiang (European journal of human genetics : EJHG, 2020)
Keywords: Antisense oligonucleotides; Dystrophin; Exon skipping; Ribonucleic acid; RNA; Splicing