Genetically modified adipose tissue-derived stem/stromal cells, using simian immunodeficiency virus-based lentiviral vectors, in the treatment of hemophilia B - Watanabe, Natsumi; Ohashi, Kazuo; Tatsumi, Kohei; Utoh, Rie; Shim, In Kyong; Kanegae, Kazuko; Kashiwakura, Yuji; Ohmori, Tsukasa; Sakata, Yoichi; Inoue, Makoto; Hasegawa, Mamoru; Okano, Teruo (Human gene therapy, 2013)
Keywords: Adipose Tissue - cytology; Animals; Blood Coagulation; Factor IX - biosynthesis; Factor IX - genetics; Gene Order; Genetic Therapy; Genetic Vectors - genetics; Hemophilia B - blood; Hemophilia B - genetics; Hemophilia B - therapy; Humans; Male; Mesenchymal Stromal Cells - cytology; Mesenchymal Stromal Cells - metabolism; Mesenchymal Stromal Cells - ultrastructure; Mice; Simian Immunodeficiency Virus - genetics; Transduction, Genetic