Nonablative neonatal marrow transplantation attenuates functional and physical defects of β-glucuronidase deficiency - Soper, Brian W.; Lessard, Mark D.; Vogler, Carole A.; Levy, Beth; Beamer, Wesley G.; Sly, William S.; Barker, Jane E. (Blood, 2001)
Keywords: Adult; Anesthesia. Intensive care medicine. Transfusions. Cell therapy and gene therapy; Animals; Animals, Newborn; Biological and medical sciences; Bone Marrow Transplantation - methods; Bone Marrow Transplantation - standards; Bone marrow, stem cells transplantation. Graft versus host reaction; Errors of metabolism; Female; Femur - abnormalities; Femur - drug effects; Femur - pathology; Glucuronidase - deficiency; Glucuronidase - metabolism; Glucuronidase - pharmacology; Graft Survival; Humans; Lipids (lysosomal enzyme disorders, storage diseases); Male; Medical sciences; Metabolic diseases; Mice; Mice, Inbred BALB C; Mice, Mutant Strains; Mucopolysaccharidosis VII - therapy; Reproduction; Tissue Distribution; Transfusions. Complications. Transfusion reactions. Cell and gene therapy; Animal model; Stem cell; Diseases of the osteoarticular system; Hematopoietic cell; Homograft; Mucopolysaccharidosis; Enzymopathy; Enzymatic activity; Bone marrow; Graft; Carbohydrate; Pretreatment; Human; β-Glucuronidase; Enzyme; Deficiency; Rodentia; Metabolic diseases; Non myeloablative treatment; Genetic disease; Vertebrata; Chemotherapy; Mammalia; Newborn; Treatment; Mouse; Glycosidases; Animal; Hydrolases; Therapeutic protocol; O-Glycosidases