A Cross-Sectional Retrospective Study of Non-Splenectomized and Never-Treated Patients with Type 1 Gaucher Disease - Serratrice, Christine; Stirnemann, Jérôme; Berrahal, Amina; Belmatoug, Nadia; Camou, Fabrice; Caillaud, Catherine; Billette de Villemeur, Thierry; Dalbies, Florence; Cador, Bérengère; Froissart, Roseline; Masseau, Agathe; Brassier, Anaïs; et al. (Journal of clinical medicine, 2020)
Keywords: Clinical medicine; Enzymes; Hematology; Hemoglobin; Human health and pathology; Laboratories; Life Sciences; Parkinson's disease; Patients; Surveillance; Thrombocytopenia; France; United States--US; risk factors; Gaucher disease; enzyme replacement therapy; disease course; lysosomal storage disorder; prognosis