Using muscle homing peptide CyPep10 to deliver phosphorodiamidate morpholino oligomers in the mdx mouse - Schneider, Anne-Fleur E.; Tanganyika-de Winter, Christa L.; Jirka, Silvana M.G.; Tan, Xuyu; Thompson, Emily G.; Ha, Kristen; Mitra, Anindita; Garcia, Stephanie; Luimes, Marleen; Oliver, Ryan A.; Guerlavais, Vincent; Aartsma-Rus, Annemieke (Molecular therapy. Nucleic acids, 2025)
Keywords: antisense oligonucleotide; cell-penetrating peptide; cyclic peptide; Duchenne muscular dystrophy; MT: Delivery Strategies; muscle uptake; Original; PMO; muscle uptake; PMO; antisense oligonucleotide; Duchenne muscular dystrophy; cyclic peptide; MT: Delivery Strategies; cell-penetrating peptide