Modeling the multi‐state natural history of rare diseases with heterogeneous individual patient data: A simulation study - Broomfield, Jonathan; Abrams, Keith R.; Freeman, Suzanne; Latimer, Nicholas; Rutherford, Mark J.; Crowther, Michael J. (Statistics in medicine, 2024)
Keywords: multi‐state model; Natural history; Rare diseases; simulation; survival analysis; rare diseases; multi-state model; survival analysis; natural history; simulation