Impact of Nusinersen on the Health-Related Quality of Life and Caregiver Burden in Patients with Spinal Muscular Atrophy with Symptom Onset before the Age of 6 Months - Lee, Yun Jeong; Bae, Hyunwoo; Shim, Young Kyu; Cho, Jae So; Chae, Jong Hee; Kwon, Soonhak (Annals of child neurology, 2025)
Keywords: caregiver burden; nusinersen; quality of life; spinal muscular atrophies of childhood; 신경과학