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Design and Monitoring of Multi-Arm Multi-Stage Clinical Trials
Ghosh, Pranab, Liu, Lingyun, Senchaudhuri, P., Gao, Ping, Mehta, Cyrus
Published in Biometrics (01.12.2017)
Published in Biometrics (01.12.2017)
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A multi-laboratory preclinical trial in rodents to assess treatment candidates for acute ischemic stroke
Lyden, Patrick D, Diniz, Márcio A, Bosetti, Francesca, Lamb, Jessica, Nagarkatti, Karisma A, Rogatko, André, Kim, Sungjin, Cabeen, Ryan P, Koenig, James I, Akhter, Kazi, Arbab, Ali S, Avery, Brooklyn D, Beatty, Hannah E, Bibic, Adnan, Cao, Suyi, Simoes Braga Boisserand, Ligia, Chamorro, Angel, Chauhan, Anjali, Diaz-Perez, Sebastian, Dhandapani, Krishnan, Dhanesha, Nirav, Goh, Andrew, Herman, Alison L, Hyder, Fahmeed, Imai, Takahiko, Johnson, Conor W, Khan, Mohammad B, Kamat, Pradip, Karuppagounder, Senthilkumar S, Kumskova, Mariia, Mihailovic, Jelena M, Mandeville, Joseph B, Morais, Andreia, Patel, Rakesh B, Sanganahalli, Basavaraju G, Smith, Cameron, Shi, Yanrong, Sutariya, Brijesh, Thedens, Daniel, Qin, Tao, Velazquez, Sofia E, Aronowski, Jaroslaw, Ayata, Cenk, Chauhan, Anil K, Leira, Enrique C, Hess, David C, Koehler, Raymond C, McCullough, Louise D, Sansing, Lauren H
Published in Science translational medicine (20.09.2023)
Published in Science translational medicine (20.09.2023)
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Comparison of Bayesian and frequentist monitoring boundaries motivated by the Multiplatform Randomized Clinical Trial
Joo, Jungnam, Leifer, Eric S, Proschan, Michael A, Troendle, James F, Reynolds, Harmony R, Hade, Erinn A, Lawler, Patrick R, Kim, Dong-Yun, Geller, Nancy L
Published in Clinical trials (London, England) (01.12.2024)
Published in Clinical trials (London, England) (01.12.2024)
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Multi-arm multi-stage clinical trials for time-to-event outcomes
Dixit, Vaidehi, Mitra, Priyam, Simonsen, Katy
Published in Journal of biopharmaceutical statistics (02.11.2021)
Published in Journal of biopharmaceutical statistics (02.11.2021)
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Choice of futility boundaries for group sequential designs with two endpoints
Schüler, Svenja, Kieser, Meinhard, Rauch, Geraldine
Published in BMC medical research methodology (08.08.2017)
Published in BMC medical research methodology (08.08.2017)
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Optimality criteria for futility stopping boundaries for group sequential designs with a continuous endpoint
Li, Xieran, Herrmann, Carolin, Rauch, Geraldine
Published in BMC medical research methodology (05.11.2020)
Published in BMC medical research methodology (05.11.2020)
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Simultaneous sequential monitoring of efficacy and safety led to masking of effects
van Eekelen, Rik, de Hoop, Esther, van der Tweel, Ingeborg
Published in Journal of clinical epidemiology (01.08.2016)
Published in Journal of clinical epidemiology (01.08.2016)
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Adaptive group‐sequential design with population enrichment in phase 3 randomized controlled trials with two binary co‐primary endpoints
Sinha, Arup K., Moye, Lemuel, Piller, Linda B., Yamal, Jose‐Miguel, Barcenas, Carlos H., Lin, Jianchang, Davis, Barry R.
Published in Statistics in medicine (20.09.2019)
Published in Statistics in medicine (20.09.2019)
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Phase IV adaptive randomised clinical trials evaluating efficacy and cost-efficacy of pre-emptive pharmacogenetic genotyping strategies in the Spanish National Health System: iPHARMGx Master Protocol and PREVESTATGx nested clinical trial
Stewart, Stefan, Seco-Meseguer, Enrique, Diago-Sempere, Elena, Marín-Candón, Alicia, Carmona, Montserrat, Estébanez, Miriam, López-Fernández, Luis A, Imaz-Iglesia, Iñaki, del Mar García Saiz, María, Laserna-Mendieta, Emilio J, Peiró, Ana M, Farré, Magí, Rodriguez-Jimenez, Consuelo, Saiz-Rodriguez, Miriam, Sanabria-Cabrera, Judith, Rosas-Alonso, Rocío, Abad-Santos, Francisco, Pedrosa, Lucia, Carcas, Antonio J, García García, Irene, Borobia, Alberto M, Bernardino, Ignacio, Guiijarro-Eguinoa, Javier, Gómez López De Las Huertas, Arturo, Arias, Pedro, Martín-López, Susana, Hladun Alvaro, Olga, Arrate, Vicente, Fries, Ana, Cubo, Esther, Rodriguez Díaz, Daniel, Marqués García, Fernando, Alonso Pedrol, Núria, Maestre Muñiz, Modesto M, Rodríguez Alcolado, Leticia, García-González, Xandra, Ortiz-Bautista, Carlos, Remesal-Doblado, Angela, Lucena, María Isabel, Salmón González, Zaida, Taladriz-Sender, Irene, Coca-Prieto, Inmaculada
Published in BMJ open (07.11.2024)
Published in BMJ open (07.11.2024)
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Comparison of Bayesian vs Frequentist Adaptive Trial Design in the Stroke Hyperglycemia Insulin Network Effort Trial
Broglio, Kristine, Meurer, William J., Durkalski, Valerie, Pauls, Qi, Connor, Jason, Berry, Donald, Lewis, Roger J., Johnston, Karen C., Barsan, William G.
Published in JAMA network open (11.05.2022)
Published in JAMA network open (11.05.2022)
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Bayesian dynamic borrowing in group-sequential design for medical device studies
Chiaruttini, Maria Vittoria, Lorenzoni, Giulia, Gregori, Dario
Published in BMC medical research methodology (20.03.2025)
Published in BMC medical research methodology (20.03.2025)
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A phase 2 study to evaluate efficacy and safety of PRGN-2009, a novel gorilla adenovirus-based immunotherapy, in combination with pembrolizumab versus pembrolizumab monotherapy in patients with recurrent or metastatic cervical cancer
Birrer, Michael J., Liao, John B., Lankford, Amy, Disis, Mary L., Gulley, James L.
Published in Journal of clinical oncology (01.06.2024)
Published in Journal of clinical oncology (01.06.2024)
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