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Published in Molecular therapy. Methods & clinical development (01.01.2016)
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The clinical landscape for AAV gene therapies
Kuzmin, Dmitry A, Shutova, Maria V, Johnston, Natalie R, Smith, Owen P, Fedorin, Vasily V, Kukushkin, Yury S, van der Loo, Johannes C M, Johnstone, Elaine C
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Critical Variables Affecting Clinical-Grade Production of the Self-Inactivating Gamma-Retroviral Vector for the Treatment of X-linked Severe Combined Immunodeficiency
van der Loo, Johannes CM, Swaney, William P, Grassman, Elke, Terwilliger, Ami, Higashimoto, Tomoyasu, Schambach, Axel, Hacein-Bey-Abina, Salima, Nordling, Diana L, Cavazzana-Calvo, Marina, Thrasher, Adrian J, Williams, David A, Reeves, Lilith, Malik, Punam
Published in Molecular therapy (01.09.2012)
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Published in Molecular therapy (01.09.2012)
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Stable Multilineage Hematopoietic Chimerism in α-Thalassemic Mice Induced by a Bone Marrow Subpopulation That Excludes the Majority of Day-12 Spleen Colony-Forming Units
van der Loo, Johannes CM, van den Bos, Cor, Baert, Miranda R.M., Wagemaker, Gerard, Ploemacher, Rob E.
Published in Blood (01.04.1994)
Published in Blood (01.04.1994)
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