Transformative effect of a Humanitarian Program for individuals affected by rare diseases: building support systems and creating local expertise
Verma, I C, El-Beshlawy, A, Tylki-Szymańska, A, Martins, A, Duan, Y-L, Collin-Histed, T, van der Linde, M Schoneveld, Mansour, R, Dũng, V C, Mistry, Pramod K
Published in Orphanet journal of rare diseases (04.04.2022)
Published in Orphanet journal of rare diseases (04.04.2022)
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Journal Article