The expanded CAG repeat in the huntingtin gene as target for therapeutic RNA modulation throughout the HD mouse brain
Datson, Nicole A, González-Barriga, Anchel, Kourkouta, Eleni, Weij, Rudie, van de Giessen, Jeroen, Mulders, Susan, Kontkanen, Outi, Heikkinen, Taneli, Lehtimäki, Kimmo, van Deutekom, Judith C T
Published in PloS one (09.02.2017)
Published in PloS one (09.02.2017)
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Design and Analysis of Effects of Triplet Repeat Oligonucleotides in Cell Models for Myotonic Dystrophy
González-Barriga, Anchel, Mulders, Susan AM, van de Giessen, Jeroen, Hooijer, Jeroen D, Bijl, Suzanne, van Kessel, Ingeborg DG, van Beers, Josee, van Deutekom, Judith CT, Fransen, Jack AM, Wieringa, Bé, Wansink, Derick G
Published in Molecular therapy. Nucleic acids (01.03.2013)
Published in Molecular therapy. Nucleic acids (01.03.2013)
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Abstracts7th Annual Meeting of the Oligonucleotide Therapeutics SocietyCopenhagen, DenmarkSeptember 8–10, 2011
Aartsma-Rus, Annemieke, Karnaoek, Tatyana, I, Bestel, Leatherbury, Neil, SA, Schwabe, J, Hunziker, Rockey, William M, Spencer, David M, Giangrande, Paloma H, Tavitian, Bertrand, Kjems, Jørgen, Bolcato-Bellemin, Anne-Laure, Deglane, Gaëlle, Goldeck, M., Schuberth, C., van Kessel, Ingeborg, Hartmann, Roland K., Hall, Jonathan, Gait, Michael J, Hornung, Veit, Hartmann, Gunther, Schlee, Martin, MW, Lindholm, Veedu, Rakesh N., Harbottle, R., Kazakov, S. A., NarayanannairJayaprakash, K., Wang, Gang, Sah, Dinah W.Y., Manoharan, Muthiah, Nielsen, Niels Fisker, Kauppinen, Sakari, Elmén, Joacim, Fettes, Kevin, Sobczak, Milena, Kim, Hee Won, Svrzikapa, Nenad, Qin, June, Tracy, Mark A., Makita, Naoki, Nagahara, Shunji, Stockdale, Katie R., Hanin, Geula, Gilboa-Geffen, Adi, Soreq, Hermona, McClorey, Graham, Shibata, Atsushi, Kummer, Ursula, Nawrot, Barbara, Snead, Nicholas M., Kamiya, D., Matsui, Yuriko, Tran, Phong Lan Thao, Rayner, Bernard, Urban, Johannes, Phua, Kyle Kok Loong, Harada-Shiba, Mariko, Obika, Satoshi, Agapkina, J., Aouadi, Myriam, Guo, Chang-An, Byun, Jonghoe, Tula, Saison-Behmoaras, Galun, Eithan, M, Yamamoto, Iversen, Patrick, Kim, Sera, Komoriya, Akira, Nagatsugi, Fumi, Kusano, Shuhei, Mohri, Kohta, Bernhard, Noll, Philipp, Hadwiger, Shrewsbury, Stephen, Takahashi, Mayumi, Matsuda, Akira, Sah, D.W., Gantier, Michael P., Sczakiel, Georg, C., Coch, B., Kümmerer, S., Herberhold, G., Kochs, M., Schlee, Trujillo, Robin Deis, Edbrooke, Mark, Fitzgerald-Bocarsly, Patricia, Gibson, Neil W., Bhat, Balkrishen, Chen, Hubert, Jackson, Aimee L., A, Buchbinder, Hawkins, Philip, Cehelsky, Jeff, Gollob, Jared, Moore, Michael D., Chomchan, Pritsana, Hua, Yimin, Sahashi, Kentaro, Aarts, Marieke
Published in Nucleic acid therapeutics (01.10.2011)
Published in Nucleic acid therapeutics (01.10.2011)
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