Beclin‐1‐mediated activation of autophagy improves proximal and distal urea cycle disorders
Soria, Leandro R, Gurung, Sonam, De Sabbata, Giulia, Perocheau, Dany P, De Angelis, Angela, Bruno, Gemma, Polishchuk, Elena, Paris, Debora, Cuomo, Paola, Motta, Andrea, Orford, Michael, Khalil, Youssef, Eaton, Simon, Mills, Philippa B, Waddington, Simon N, Settembre, Carmine, Muro, Andrés F, Baruteau, Julien, Brunetti‐Pierri, Nicola
Published in EMBO molecular medicine (05.02.2021)
Published in EMBO molecular medicine (05.02.2021)
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Journal Article
Long-term correction of ornithine transcarbamylase deficiency in Spf-Ash mice with a translationally optimized AAV vector
De Sabbata, Giulia, Boisgerault, Florence, Guarnaccia, Corrado, Iaconcig, Alessandra, Bortolussi, Giulia, Collaud, Fanny, Ronzitti, Giuseppe, Sola, Marcelo Simon, Vidal, Patrice, Rouillon, Jeremy, Charles, Severine, Nicastro, Emanuele, D’Antiga, Lorenzo, Ilyinskii, Petr, Mingozzi, Federico, Kishimoto, Takashi Kei, Muro, Andrés F.
Published in Molecular therapy. Methods & clinical development (12.03.2021)
Published in Molecular therapy. Methods & clinical development (12.03.2021)
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Journal Article
Long-term correction of ornithine transcarbamylase deficiency in Spf-Ash mice with a translationally optimized AAV vector
de Sabbata, Giulia, Boisgerault, Florence, Guarnaccia, Corrado, Iaconcig, Alessandra, Bortolussi, Giulia, Collaud, Fanny, Ronzitti, Giuseppe, Sola, Marcelo Simon, Vidal, Patrice, Rouillon, Jeremy, Charles, Severine, Nicastro, Emanuele, D’antiga, Lorenzo, Ilyinskii, Petr, Mingozzi, Federico, Kishimoto, Takashi Kei, Muro, Andrés
Published in Molecular therapy. Methods & clinical development (01.03.2021)
Published in Molecular therapy. Methods & clinical development (01.03.2021)
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Journal Article
METHODS AND COMPOSITIONS OF OTC CONSTRUCTS AND VECTORS
De Sabbata, Giulia, Kishimoto, Takashi Kei, Muro, Andres, Keller, Peter
Year of Publication 06.02.2020
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Year of Publication 06.02.2020
Patent
Beclin-1-mediated activation of autophagy improves proximal and distal urea cycle disorders
Soria, Leandro R, Perocheau, Dany P, De Sabbata, Giulia, De Angelis, Angela, Bruno, Gemma, Polishchuk, Elena, Gurung, Sonam, Paris, Debora, Cuomo, Paola, Motta, Andrea, Orford, Michael, Eaton, Simon, Waddington, Simon, Settembre, Carmine, Muro, Andres F, Baruteau, Julien, Brunetti-Pierri, Nicola
Published in bioRxiv (24.07.2020)
Published in bioRxiv (24.07.2020)
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Paper
METHODS AND COMPOSITIONS OF OTC CONSTRUCTS AND VECTORS
DE SABBATA, Giulia, KISHIMOTO, Takashi, Kei, MURO, Andres, KELLER, Peter
Year of Publication 26.05.2021
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Year of Publication 26.05.2021
Patent
Methods and compositions of OTC constructs and vectors
KISHIMOTO, Takashi Kei, DE SABBATA, Giulia, MURO, Andres, KELLER, Peter
Year of Publication 28.01.2021
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Year of Publication 28.01.2021
Patent
METHODS AND COMPOSITIONS OF OTC CONSTRUCTS AND VECTORS
KISHIMOTO, TAKASHI KEI, MURO, ANDRES, KELLER, PETER, DE SABBATA, GIULIA
Year of Publication 23.01.2020
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Year of Publication 23.01.2020
Patent