Disease duration and survival in Brazilian Niemann-Pick disease type C patients: Preliminary data on potential impact of miglustat
Giugliani, Luciana, Van der Linder, Vanesa, Van Der Linden, Helio, Lourenço, Charles Marques, de Araújo Leão, Emília Katiane Embiruçu, Arita, Juliana Harumi, Doriqui, Maria Julia Rodovalho, Neto, Pedro Braga, de Souza, Carolina Fischinger Moura, Horovitz, Dafne Dain Gandelman, Santos, Mara Lucia, Grillo, Eugenio, da Silva, Raquel Tavares Boy, de Oliveira Abrão, Janaina Bianca, Trapp, Franciele Barbosa, Giugliani, Roberto
Published in Molecular genetics and metabolism (01.02.2016)
Published in Molecular genetics and metabolism (01.02.2016)
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