Next generation triplex-forming PNAs for site-specific genome editing of the F508del CFTR mutation
Gupta, Anisha, Barone, Christina, Quijano, Elias, Piotrowski-Daspit, Alexandra S., Perera, J. Dinithi, Riccardi, Adele, Jamali, Haya, Turchick, Audrey, Zao, Weixi, Saltzman, W. Mark, Glazer, Peter M., Egan, Marie E.
Published in Journal of cystic fibrosis (05.08.2024)
Published in Journal of cystic fibrosis (05.08.2024)
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