Dual mRNA therapy restores metabolic function in long-term studies in mice with propionic acidemia
Jiang, Lei, Park, Ji-Sun, Yin, Ling, Laureano, Rodrigo, Jacquinet, Eric, Yang, Jinsong, Liang, Shi, Frassetto, Andrea, Zhuo, Jenny, Yan, Xinhua, Zhu, Xuling, Fortucci, Steven, Hoar, Kara, Mihai, Cosmin, Tunkey, Christopher, Presnyak, Vlad, Benenato, Kerry E., Lukacs, Christine M., Martini, Paolo G. V., Guey, Lin T.
Published in Nature communications (21.10.2020)
Published in Nature communications (21.10.2020)
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Lipid nanoparticle-targeted mRNA therapy as a treatment for the inherited metabolic liver disorder arginase deficiency
Truong, Brian, Allegri, Gabriella, Liu, Xiao-Bo, Burke, Kristine E., Zhu, Xuling, Cederbaum, Stephen D., Häberle, Johannes, Martini, Paolo G. V., Lipshutz, Gerald S.
Published in Proceedings of the National Academy of Sciences - PNAS (15.10.2019)
Published in Proceedings of the National Academy of Sciences - PNAS (15.10.2019)
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Systemic mRNA Therapy for the Treatment of Fabry Disease: Preclinical Studies in Wild-Type Mice, Fabry Mouse Model, and Wild-Type Non-human Primates
Zhu, Xuling, Yin, Ling, Theisen, Matt, Zhuo, Jenny, Siddiqui, Summar, Levy, Becca, Presnyak, Vladimir, Frassetto, Andrea, Milton, Jaclyn, Salerno, Timothy, Benenato, Kerry E., Milano, Joe, Lynn, Andy, Sabnis, Staci, Burke, Kristine, Besin, Gilles, Lukacs, Christine M., Guey, Lin T., Finn, Patrick F., Martini, Paolo G.V.
Published in American journal of human genetics (04.04.2019)
Published in American journal of human genetics (04.04.2019)
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Journal Article
Systemic Messenger RNA Therapy as a Treatment for Methylmalonic Acidemia
An, Ding, Schneller, Jessica L., Frassetto, Andrea, Liang, Shi, Zhu, Xuling, Park, Ji-Sun, Theisen, Matt, Hong, Sue-Jean, Zhou, Jenny, Rajendran, Raj, Levy, Becca, Howell, Rebecca, Besin, Gilles, Presnyak, Vladimir, Sabnis, Staci, Murphy-Benenato, Kerry E., Kumarasinghe, E. Sathyajith, Salerno, Timothy, Mihai, Cosmin, Lukacs, Christine M., Chandler, Randy J., Guey, Lin T., Venditti, Charles P., Martini, Paolo G.V.
Published in Cell reports (Cambridge) (19.12.2017)
Published in Cell reports (Cambridge) (19.12.2017)
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WGCNA and transcriptome profiling reveal hub genes for key development stage seed size/oil content between wild and cultivated soybean
Yao, Yanjie, Xiong, Erhui, Qu, Xuelian, Li, Junfeng, Liu, Hongli, Quan, Leipo, Lu, Wenyan, Zhu, Xuling, Chen, Meiling, Li, Ke, Chen, Xiaoming, Lian, Yun, Lu, Weiguo, Zhang, Dan, Zhou, Xinan, Chu, Shanshan, Jiao, Yongqing
Published in BMC genomics (28.08.2023)
Published in BMC genomics (28.08.2023)
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Systemic modified messenger RNA for replacement therapy in alpha 1-antitrypsin deficiency
Karadagi, Ahmad, Cavedon, Alex G, Zemack, Helen, Nowak, Greg, Eybye, Marianne E, Zhu, Xuling, Guadagnin, Eleonora, White, Rebecca A, Rice, Lisa M, Frassetto, Andrea L, Strom, Stephen, Jorns, Carl, Martini, Paolo G V, Ellis, Ewa
Published in Scientific reports (27.04.2020)
Published in Scientific reports (27.04.2020)
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Diphthamide biosynthesis requires an organic radical generated by an iron–sulphur enzyme
Ealick, Steven E, Lin, Hening, Zhang, Yang, Zhu, Xuling, Torelli, Andrew T, Lee, Michael, Dzikovski, Boris, Koralewski, Rachel M, Wang, Eileen, Freed, Jack, Krebs, Carsten
Published in Nature (London) (17.06.2010)
Published in Nature (London) (17.06.2010)
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Comparisons of constitutive resistances to soybean cyst nematode between PI 88788- and Peking-type sources of resistance in soybean by transcriptomic and metabolomic profilings
Chu, Shanshan, Ma, Hui, Li, Ke, Li, Junfeng, Liu, Hongli, Quan, Leipo, Zhu, Xuling, Chen, Meiling, Lu, Wenyan, Chen, Xiaoming, Qu, Xuelian, Xu, Jiaqi, Lian, Yun, Lu, Weiguo, Xiong, Erhui, Jiao, Yongqing
Published in Frontiers in genetics (10.11.2022)
Published in Frontiers in genetics (10.11.2022)
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Intermittent lipid nanoparticle mRNA administration prevents cortical dysmyelination associated with arginase deficiency
Khoja, Suhail, Liu, Xiao-Bo, Truong, Brian, Nitzahn, Matthew, Lambert, Jenna, Eliav, Adam, Nasser, Eram, Randolph, Emma, Burke, Kristine E., White, Rebecca, Zhu, Xuling, Martini, Paolo G.V., Nissim, Itzhak, Cederbaum, Stephen D., Lipshutz, Gerald S.
Published in Molecular therapy. Nucleic acids (14.06.2022)
Published in Molecular therapy. Nucleic acids (14.06.2022)
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Identification of ADP-ribosylation sites of CD38 mutants by precursor ion scanning mass spectrometry
Jiang, Hong, Sherwood, Robert, Zhang, Sheng, Zhu, Xuling, Liu, Qun, Graeff, Richard, Kriksunov, Irina A., Lee, Hon Cheung, Hao, Quan, Lin, Hening
Published in Analytical biochemistry (15.02.2013)
Published in Analytical biochemistry (15.02.2013)
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Systemic messenger RNA as an etiological treatment for acute intermittent porphyria
Jiang, Lei, Berraondo, Pedro, Jericó, Daniel, Guey, Lin T, Sampedro, Ana, Frassetto, Andrea, Benenato, Kerry E, Burke, Kristine, Santamaría, Eva, Alegre, Manuel, Pejenaute, Álvaro, Kalariya, Mayur, Butcher, William, Park, Ji-Sun, Zhu, Xuling, Sabnis, Staci, Kumarasinghe, E Sathyajith, Salerno, Timothy, Kenney, Matthew, Lukacs, Christine M, Ávila, Matías A, Martini, Paolo G V, Fontanellas, Antonio
Published in Nature medicine (01.12.2018)
Published in Nature medicine (01.12.2018)
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Effects of Dietary 5'-CMP on Neu5Gc Contents in the Muscle and Viscera of Xiang Pigs
Li, Hongying, Zhu, Qiujin, Chang, Rui, Hu, K E, Zhu, Xuling, Xu, Aqi, Xu, Shitao, Tang, Pengyu
Published in Journal of food protection (01.01.2021)
Published in Journal of food protection (01.01.2021)
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Dph3 Is an Electron Donor for Dph1-Dph2 in the First Step of Eukaryotic Diphthamide Biosynthesis
Dong, Min, Su, Xiaoyang, Dzikovski, Boris, Dando, Emily E, Zhu, Xuling, Du, Jintang, Freed, Jack H, Lin, Hening
Published in Journal of the American Chemical Society (05.02.2014)
Published in Journal of the American Chemical Society (05.02.2014)
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AtMYBS1 negatively regulates heat tolerance by directly repressing the expression of MAX1 required for strigolactone biosynthesis in Arabidopsis
Li, Xiang, Lu, Jianhua, Zhu, Xuling, Dong, Yanqi, Liu, Yanli, Chu, Shanshan, Xiong, Erhui, Zheng, Xu, Jiao, Yongqing
Published in Plant communications (13.11.2023)
Published in Plant communications (13.11.2023)
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GNF-2 Inhibits Dengue Virus by Targeting Abl Kinases and the Viral E Protein
Clark, Margaret J., Miduturu, Chandra, Schmidt, Aaron G., Zhu, Xuling, Pitts, Jared D., Wang, Jinhua, Potisopon, Supanee, Zhang, Jianming, Wojciechowski, Amy, Hann Chu, Justin Jang, Gray, Nathanael S., Yang, Priscilla L.
Published in Cell chemical biology (21.04.2016)
Published in Cell chemical biology (21.04.2016)
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Reconstitution of Diphthine Synthase Activity in Vitro
Zhu, Xuling, Kim, Jungwoo, Su, Xiaoyang, Lin, Hening
Published in Biochemistry (Easton) (09.11.2010)
Published in Biochemistry (Easton) (09.11.2010)
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Journal Article
Effects of Dietary Cytidine 5'-monophosphate on Neu5Gc contents in the Muscle and Viscera of Xiang Pigs
Li, Hongying, Zhu, Qiujing, Chang, Rui, Hu, Ke, Zhu, Xuling, Xu, Aqi, Xu, Shitao, Tang, Pengyu
Published in Journal of food protection (07.08.2020)
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Published in Journal of food protection (07.08.2020)
Journal Article
Systemic Messenger RNA Therapy as a Treatment for Methylmalonic Acidemia
An, Ding, Schneller, Jessica L., Frassetto, Andrea, Liang, Shi, Zhu, Xuling, Park, Ji-Sun, Theisen, Matt, Hong, Sue-Jean, Zhou, Jenny, Rajendran, Raj, Levy, Becca, Howell, Rebecca, Besin, Gilles, Presnyak, Vladimir, Sabnis, Staci, Murphy-Benenato, Kerry E., Kumarasinghe, E. Sathyajith, Salerno, Timothy, Mihai, Cosmin, Lukacs, Christine M., Chandler, Randy J., Guey, Lin T., Venditti, Charles P., Martini, Paolo G.V.
Published in Cell reports (Cambridge) (28.08.2018)
Published in Cell reports (Cambridge) (28.08.2018)
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