Intravenous administration of an AAV-2 vector for the expression of factor IX in mice and a dog model of hemophilia B
HARDING, T. C, KOPRIVNIKAR, K. E, NICHOLS, T. C, BELLINGER, D. A, YENDLURI, S, WAUGH, J, MCARTHUR, J, VERES, G, DONAHUE, B. A, TU, G. H, ZAYEK, N, LEW, S, SUBRAMANIAN, A, SIVAKUMARAN, A, FREY, D, HO, K, VANROEY, M. J
Published in Gene therapy (01.01.2004)
Published in Gene therapy (01.01.2004)
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Production of human clotting Factor IX without toxicity in mice after vascular delivery of a lentiviral vector
McArthur, James G, Tsui, Lisa V, Kelly, Michael, Zayek, Nathalie, Rojas, Virginia, Ho, Ken, Ge, Ying, Moskalenko, Marina, Mondesire, Jean, Davis, Jennifer, Roey, Melinda Van, Dull, Tom
Published in Nature biotechnology (01.01.2002)
Published in Nature biotechnology (01.01.2002)
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Development of a sensitive assay for detection of replication-competent recombinant lentivirus in large-scale HIV-based vector preparations
Escarpe, Paul, Zayek, Nathalie, Chin, Peggy, Borellini, Flavia, Zufferey, Romain, Veres, Gabor, Kiermer, Veronique
Published in Molecular therapy (01.08.2003)
Published in Molecular therapy (01.08.2003)
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p27-p16 Fusion Gene Inhibits Angioplasty-Induced Neointimal Hyperplasia and Coronary Artery Occlusion
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Published in Circulation research (17.08.2001)
Published in Circulation research (17.08.2001)
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Stability of Adenoviral Vectors Following Catheter Delivery
Tsui, Lisa V., Zayek, Nathalie, Frey, David, Mello, Christopher, Banik, Gautam, Falotico, Robert, McArthur, James G.
Published in Molecular therapy (01.01.2001)
Published in Molecular therapy (01.01.2001)
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