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Published in Journal of lipid research (01.11.2017)
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Published in PloS one (07.04.2015)
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Published in Hepatology communications (01.06.2020)
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Published in Gene therapy (01.09.2022)
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Optimization of base editors for the functional correction of SMN2 as a treatment for spinal muscular atrophy
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Published in Nature biomedical engineering (01.02.2024)
Published in Nature biomedical engineering (01.02.2024)
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Radiological and Pathological Features Associated with IDH1-R132H Mutation Status and Early Mortality in Newly Diagnosed Anaplastic Astrocytic Tumours: e0123890
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Published in PloS one (01.04.2015)
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Base editing as a genetic treatment for spinal muscular atrophy
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Published in bioRxiv : the preprint server for biology (21.01.2023)
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Published in bioRxiv : the preprint server for biology (21.01.2023)
Journal Article
Base editing as a genetic treatment for spinal muscular atrophy
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Published in bioRxiv (21.01.2023)
Published in bioRxiv (21.01.2023)
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