Vyzkoušejte nový nástroj s podporou AI
Summon Research Assistant
BETA
Loading…
Long-term outcome in Wiskott-Aldrich syndrome and X-linked thrombocytopenia patients: an observational -prospective multi-center study of the Italian Primary Immune Deficiency Network (IPINET)
Soresina, Annarosa, Rondelli, Roberto, Notarangelo, Lucia Dora, Locatelli, Franco, Aiuti, Alessandro, Biffi, Alessandra, Rabusin, Marco, Pignata, Claudio, Menna, Giuseppe, Prete, Arcangelo, Faraci, Maura, Rovelli, Attilio, Conti, Francesca, Bertolini, Patrizia, Azzari, Chiara, Cancrini, Caterina, Zecca, Marco, Ferrua, Francesca, Cicalese, Maria Pia, Cecere, Francesco, Dotta, Laura, Martire, Baldassarre, Giliani, Silvia, Moratto, Daniele, Mazza, Cinzia, Plebani, Alessandro, Notarangelo, Luigi D., Pession, Andrea, Badolato, Raffaele, Porta, Fulvio
Published in EClinicalMedicine (01.06.2025)
Published in EClinicalMedicine (01.06.2025)
Get full text
Journal Article
Loading…
Long-term outcome in Wiskott-Aldrich syndrome and X-linked thrombocytopenia patients: an observational -prospective multi-center study of the Italian Primary Immune Deficiency Network (IPINET)Research in context
Annarosa Soresina, Roberto Rondelli, Lucia Dora Notarangelo, Franco Locatelli, Alessandro Aiuti, Alessandra Biffi, Marco Rabusin, Claudio Pignata, Giuseppe Menna, Arcangelo Prete, Maura Faraci, Attilio Rovelli, Francesca Conti, Patrizia Bertolini, Chiara Azzari, Caterina Cancrini, Marco Zecca, Francesca Ferrua, Maria Pia Cicalese, Francesco Cecere, Laura Dotta, Baldassarre Martire, Silvia Giliani, Daniele Moratto, Cinzia Mazza, Alessandro Plebani, Luigi D. Notarangelo, Andrea Pession, Raffaele Badolato, Fulvio Fulvio
Published in EClinicalMedicine (01.06.2025)
Published in EClinicalMedicine (01.06.2025)
Get full text
Journal Article
Loading…
Effects Of Eltrombopag On Thrombocytopenia, Platelet Function and Bleeding In Patients With Wiskott-Aldrich Syndrome/X-Linked Thrombocytopenia
Gerrits, Anja J, Leven, Emily, Frelinger, Andrew L., Berny-Lang, Michelle A., Tamary, Hannah, Revel-Vilk, Shoshana, Carmichael, Sabrina L., Mitchell, W. Beau, Michelson, Alan D., Bussel, James B
Published in Blood (15.11.2013)
Published in Blood (15.11.2013)
Get full text
Journal Article
Loading…
Therapeutic genome editing in Wiskott-Aldrich syndrome and X-linked thrombocytopenia
Year of Publication 09.05.2023
Get full text
Patent
Loading…
Hereditary X-Linked Thrombocytopenia Maps to the Same Chromosomal Region as the Wiskott-Aldrich Syndrome
Donner, Mikael, Schwartz, Marianne, Carlsson, Karin Utas, Holmberg, Lars
Published in Blood (01.12.1988)
Published in Blood (01.12.1988)
Get full text
Journal Article
Loading…
THERAPEUTIC GENOME EDITING IN WISKOTT-ALDRICH SYNDROME AND X-LINKED THROMBOCYTOPENIA
Year of Publication 19.04.2018
Get full text
Patent
Loading…
Inborn Error of WAS Presenting with SARS-CoV-2-Related Multisystem Inflammatory Syndrome in Children
Drago, Enrico, Fioredda, Francesca, Penco, Federica, Prigione, Ignazia, Bertoni, Arinna, Del Zotto, Genny, Bocca, Paola, Massaccesi, Erika, Lanciotti, Marina, Moratto, Daniele, Thurner, Lorenz, Caorsi, Roberta, Gattorno, Marco, Volpi, Stefano
Published in Journal of clinical immunology (01.12.2025)
Published in Journal of clinical immunology (01.12.2025)
Get full text
Journal Article